Ultragenyx Announces U.S. FDA Approval of GENGLYCOS™ Gene Therapy, the First-Ever FDA-Approved Treatment Designed to Treat the Underlying Cause of [...]

Spring 2026 Newsletter The Conference Edition View Newsletter

Winter 2026 Ultragenyx Update n February, Ultragenyx announced the U.S. FDA granted Priority Review for the Biologics License Application [...]

Ultragenyx Update: DTX401 BLA Accepted The U.S. FDA has granted Priority Review for the Biologics License Application (BLA) for our [...]

Ultragenyx GSD1A Community Update Fall 2025 DTX401 program updates and global community engagement highlights. View Community Update [...]

Fall 2025 Newsletter AGSD Annual Conference 2025 – A Resounding Success! This past June, the AGSD community gathered in [...]