Survey for our Type II GSD - Pompe Disease - patient families
This is a survey intended for patients with Lysosomal Storage Diseases. It is part of a research study to investigate LSD patients' perception of their treatment. It will ask your opinion about the use of Enzyme Replacement Therapy (ERT).
The Survey will take approximately 15 min to complete and we would be very grateful if you could help us by completing it. All surveys are anonymous and no information will be linked to you.
Lauren Zeitels, MD., PhD.